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Chronic inflammatory demyelinating polyneuropathy


Chronic inflammatory demyelinating polyneuropathy (CIDP) is an acquired immune-mediated of the peripheral characterized by progressive symmetrical weakness, sensory impairment, and areflexia due to segmental demyelination of peripheral and nerve roots. The condition typically evolves over a period exceeding eight weeks, differentiating it from acute inflammatory neuropathies such as Guillain-Barré syndrome.
CIDP exhibits a male predominance with a 2:1 ratio and increases in incidence with age, with a mean onset around 60 years, though it can affect children. Estimated ranges from 0.8 to 8.9 per 100,000 individuals, while pooled incidence is approximately 0.33 per 100,000 person-years. Most cases are idiopathic, though associations with infections, connective tissue diseases like systemic lupus erythematosus, and viral infections such as or hepatitis C have been reported. Pathophysiologically, it involves T-cell and macrophage-mediated targeting sheaths, leading to demyelination, attempted remyelination, and potential secondary axonal loss. Clinically, patients present with proximal and distal motor weakness, paresthesias, numbness, and , with sensory deficits more pronounced for vibration and than or temperature. relies on clinical , electrodiagnostic studies demonstrating prolonged motor latencies and conduction blocks, cerebrospinal fluid analysis showing elevated protein without pleocytosis, and sometimes nerve biopsy confirming demyelination. The 2021 European Federation of Neurological Societies/Peripheral Nerve Society criteria offer 83% sensitivity and 94% specificity. First-line treatments include intravenous immunoglobulin (IVIG) at 2 g/kg induction, corticosteroids, or plasma exchange, with most patients responding and approximately 40% achieving remission; maintenance often involves steroid-sparing immunosuppressants like . Despite effective therapies, diagnostic challenges persist, with misdiagnosis rates up to 54%, particularly in atypical variants.

Historical background

Initial descriptions and recognition

Cases consistent with chronic inflammatory demyelinating polyneuropathy (CIDP) were reported as early as the mid-20th century, often described as recurring or relapsing forms of distinct from acute conditions like Guillain-Barré syndrome (GBS). In 1958, J.H. Austin detailed patients with a fluctuating motor-sensory neuropathy characterized by progressive weakness, sensory loss, elevated (CSF) protein, and responsiveness to corticosteroid therapy, though without definitive pathological correlation at the time. These early observations highlighted chronic progression over weeks to months, contrasting with GBS's rapid onset within four weeks, but lacked systematic distinction or inflammatory evidence from nerve biopsies. Parallel advancements in animal modeling supported recognition of immune-mediated mechanisms underlying chronic demyelination. In 1955, Byron H. Waksman and Raymond D. Adams induced experimental allergic neuritis (EAN) in rabbits by injecting homogenized peripheral tissue emulsified with , resulting in inflammatory infiltrates, segmental demyelination, and clinical paralysis mimicking human polyneuropathies. This model, refined through the 1950s and 1960s across species like pigs and mice, demonstrated T-cell driven immune attacks on sheaths, providing causal evidence for inflammation's role in peripheral demyelination and influencing interpretations of human biopsy findings showing perivascular infiltrates and onion-bulb formations. The formal identification of CIDP as a distinct entity occurred in 1975, when Peter J. Dyck and colleagues at Mayo Clinic analyzed 53 patients from a cohort of chronic idiopathic polyneuropathies, defining it as a symmetric sensorimotor disorder with progression exceeding eight weeks, proximal and distal weakness, areflexia, elevated CSF protein without pleocytosis, and nerve conduction slowing. Pathological examination of sural nerve biopsies in 26 cases revealed prominent segmental demyelination with macrophage-mediated myelin stripping and endoneurial inflammation, though axonal degeneration affected about 25% of fibers; this differentiated CIDP from purely axonal or hereditary neuropathies and emphasized its immune-inflammatory nature akin to EAN. Initially termed "chronic inflammatory polyradiculoneuropathy," the condition was noted for potential steroid responsiveness, though not universally, solidifying its separation from acute monophasic GBS. ![CIDP histopathology showing teased fiber preparation with segmental demyelination][float-right]

Evolution of understanding and criteria

Following the initial recognition of chronic inflammatory demyelinating polyneuropathy (CIDP) in the , advancements in the and emphasized electrophysiologic techniques to differentiate demyelinating from axonal . Nerve conduction studies (NCS) identified key demyelinating features, including prolonged distal motor latencies, reduced conduction velocities exceeding 30% below lower limits of normal, prolonged F-wave latencies, and conduction or temporal dispersion in motor nerves, contrasting with axonal loss marked primarily by reduced amplitudes without such slowing. These criteria helped refine CIDP by quantifying multifocal demyelination, though early sets varied in stringency and often required confirmation for ambiguous cases. In 2010, the European Federation of Neurological Societies/Peripheral Nerve Society (EFNS/PNS) published standardized diagnostic guidelines, integrating obligatory clinical features (progressive or relapsing weakness and sensory deficits over at least 2 months), supportive electrodiagnostic evidence of demyelination in at least three , and optional cerebrospinal fluid protein elevation or nerve pathology. These criteria achieved high sensitivity (up to 99% for definite CIDP) by allowing probable or possible diagnoses with fewer abnormalities, facilitating earlier intervention while reducing misclassification of mimics like . The 2021 European Academy of Neurology/Peripheral Nerve Society (EAN/PNS) guidelines updated these by simplifying clinical requirements to definite temporal evolution (progressive or relapsing course over 8 weeks) and proximal/distal involvement, introducing a "possible CIDP" category for presentations with incomplete . Enhancements included stricter specificity for variants like distal acquired demyelinating symmetric neuropathy and sensory-predominant forms, alongside recommendations for testing in seronegative or treatment-refractory cases. Discoveries in the of autoantibodies targeting nodal and paranodal proteins, such as contactin-1 and neurofascin-155/186, informed criteria revisions by delineating subsets with paranodal disruption, often showing poor intravenous immunoglobulin response but distinct electrophysiologic patterns like uniform conduction slowing. These findings, validated in meta-analyses, prompted inclusion of serological testing in guidelines to subclassify cases beyond traditional demyelination metrics, though prevalence remains low (around 10-20% in typical CIDP).

Clinical presentation

Core signs and symptoms

Chronic inflammatory demyelinating polyneuropathy (CIDP) manifests primarily through progressive, symmetric weakness affecting both proximal and distal muscles of the upper and lower limbs, typically evolving over at least 8 weeks to distinguish it from acute forms like Guillain-Barré syndrome. This weakness often begins in the legs, leading to difficulty rising from a , climbing stairs, or walking, and may progress to involve the arms with impaired fine motor tasks such as buttoning clothing. Sensory disturbances, including numbness, tingling, and impaired vibration and position sense due to large-fiber involvement, accompany the motor deficits in most cases, though sensory symptoms are generally milder than motor ones. Deep tendon reflexes are typically absent or markedly reduced throughout, reflecting widespread and peripheral nerve dysfunction. Fatigue is a frequent complaint, exacerbating functional limitations and contributing to reduced , independent of the degree of . Gait instability arises from leg and , increasing fall risk and often necessitating assistive devices early in the course. Pain, when present, is usually neuropathic and less dominant than in axonal neuropathies, affecting a subset of patients with burning or aching sensations in affected limbs. Cranial nerve involvement occurs infrequently, with weakness reported in approximately 5-20% of cases, while bulbar or oculomotor deficits are rare. Autonomic features, such as or urinary dysfunction, appear in a minority of patients, around 25% showing mild involvement, based on clinical cohort data. These core symptoms reflect the immune-mediated demyelination targeting motor and sensory nerves, with from diagnostic cohorts confirming their predominance in typical CIDP.

Variants and atypical forms

Lewis-Sumner syndrome, also designated as multifocal acquired demyelinating sensory and motor (MADSAM) neuropathy, manifests with asymmetric, multifocal sensory and motor impairments that simulate mononeuropathy multiplex, frequently accompanied by conduction blocks on electrophysiological testing and potential evolution toward a symmetric over time. This variant affects 6-15% of CIDP cases and exhibits a less favorable response to first-line therapies compared to typical CIDP, with approximately 56% responsiveness to intravenous immunoglobulin (IVIG) and 50% to . The distal acquired demyelinating symmetric (DADS) variant features symmetric, length-dependent distal sensory or sensorimotor deficits, distinguished by markedly prolonged distal motor latencies and frequent association with IgM paraproteins in up to 50% of instances, including anti-myelin-associated glycoprotein (MAG) antibodies. Idiopathic DADS subtypes respond to standard immunomodulatory treatments like IVIG or plasma exchange in 70-80% of patients, whereas paraprotein-associated forms (DADS-M) demonstrate poorer outcomes with these agents and improved disability scores following rituximab administration. Paranodal autoantibody-mediated forms, primarily involving IgG4 antibodies targeting contactin-1 (CNTN1, prevalence 2.2-8.7%) or neurofascin-155 (NF155, 4-18%), are marked by early disease onset, prominent , , and conduction blocks, alongside axonal involvement and resistance to IVIG or corticosteroids. These subtypes, classified under autoimmune nodopathies, respond more effectively to rituximab or in refractory scenarios, reflecting distinct nodal/paranodal disruption distinct from classic cellular immune mechanisms in typical CIDP.

Etiology

Genetic and predisposing factors

Chronic inflammatory demyelinating polyneuropathy (CIDP) exhibits limited evidence of strong heritable components, with familial clustering occurring rarely and often confounded by misdiagnosis of underlying genetic neuropathies such as hereditary neuropathy with liability to pressure palsies or . Large-scale analyses indicate that CIDP susceptibility likely involves polygenic influences rather than monogenic inheritance, as twin studies and pedigree analyses show no consistent Mendelian patterns. Human leukocyte antigen (HLA) associations have been investigated, revealing modest and inconsistent links; for instance, and HLA-DR3 alleles appear elevated in some cohorts, particularly among females for DR2, with relative risks not exceeding twofold in affected populations. Other reports highlight HLA-DRB1*13 or DR3/DQ2 haplotypes in specific ethnic groups, but replication across studies is limited, and no allele confers high-penetrance risk. Genome-wide association studies (GWAS), including the first large-scale effort in 2024 analyzing over 500 CIDP cases, have identified suggestive loci such as one at 20q13.33 in females but no genome-wide significant variants replicated across sexes or ancestries, underscoring weak polygenic contributions to onset. Functional validation of candidate genes remains pending, with pathways implicating immune regulation but lacking causal confirmation. Predisposing comorbidities amplify empirical risk, notably diabetes mellitus, present in up to 20% of CIDP cases versus population baselines, potentially via hyperglycemia-induced nerve vulnerability and immune dysregulation. (MGUS), especially IgG or IgA subtypes, co-occurs in 10-20% of patients, correlating with atypical phenotypes and treatment resistance, likely through paraprotein-mediated immune perturbation without direct causality established. These associations highlight multifactorial susceptibility but do not imply , as most affected individuals lack such factors.

Triggers including infections

Antecedent infections precede the onset of chronic inflammatory demyelinating polyneuropathy (CIDP) in approximately 10% of cases, with higher rates observed among younger patients; these events often involve gastrointestinal or respiratory pathogens that trigger immune dysregulation. Documented infections include , cytomegalovirus (CMV), Epstein-Barr virus (EBV), and varicella-zoster virus (VZV), mirroring patterns seen in Guillain-Barré syndrome (GBS) but leading to a protracted course rather than acute monophasic illness. In a European collaborative study of 397 CIDP patients, infectious episodes were self-reported within 3 months prior to symptom onset in 38 cases (9.6%), predominantly viral upper respiratory infections or . The temporal association typically involves a latency period of 1-8 weeks post-infection, during which immune activation escalates into peripheral nerve targeting; acute-onset CIDP variants, comprising 16-20% of cases, may emerge within this window, progressing beyond the 8-week GBS cutoff. Longitudinal cohort data indicate that such post-infectious triggers correlate with relapsing-remitting patterns in susceptible individuals, though remains inferential due to retrospective reporting biases and lack of prospective in most series. Molecular mimicry is hypothesized as a key mechanism, wherein microbial antigens cross-react with peripheral nerve components like gangliosides or proteins, initiating autoreactive T- and B-cell responses; epitope similarity between C. jejuni lipooligosaccharides and gangliosides, well-established in GBS, extends plausibly to CIDP subsets with shared . However, direct studies in CIDP are limited, with evidence primarily extrapolated from acute demyelinating neuropathies rather than chronic cohorts, underscoring the need for targeted serological and sequencing analyses to confirm mimicry-driven triggers.

Associations with vaccinations and immune challenges

Case reports have documented instances of chronic inflammatory demyelinating polyneuropathy (CIDP) onset or exacerbation following influenza , though such events remain rare and temporally associated without established causation. The 2012 Institute of Medicine (IOM) review identified three reports of CIDP post-influenza vaccine, concluding that evidence was inadequate to accept or reject a causal relationship due to limited data and factors like underlying predisposition. Similarly, studies on symptom worsening in established CIDP patients post-flu reported rates around 20% in small cohorts, but these did not confirm vaccine-induced de novo disease. With the rollout of vaccines, clusters of CIDP cases emerged shortly after administration, primarily linked to mRNA (e.g., Pfizer-BioNTech, ) and platforms. By July 2024, at least 32 peer-reviewed case reports described CIDP following , often fulfilling diagnostic criteria like electrodiagnostic evidence of demyelination and temporal proximity (within weeks). These included pediatric cases and variants with autoantibodies (e.g., anti-NF186), but remains debated, with molecular hypothesized as a potential immune in susceptible individuals. Empirical data from surveillance systems underscore the rarity of these associations. records indicate sporadic CIDP reports post-vaccination, with incidence estimates below 1 per million doses for vaccines, far lower than background rates of CIDP (approximately 1-9 per 100,000 annually). The U.S. (NVICP) has adjudicated claims using criteria adapted from Brighton Collaboration standards for demyelinating neuropathies, awarding compensation in select CIDP cases post-influenza or other vaccines where temporal and clinical evidence supported vaccine-table injury, such as $4.4 million in a GBS-to-CIDP progression claim. These awards reflect no-fault adjudication rather than definitive proof of causation, prioritizing empirical patterns over population-level risks. Overall, while immune challenges from vaccines may unmask or precipitate CIDP in predisposed individuals via dysregulated responses, large-scale studies find no elevated population risk, emphasizing the need for individualized assessment.

Pathophysiology

Immune-mediated mechanisms

The peripheral maintains through the blood-nerve barrier (BNB), which restricts immune cell access to nerve tissues; its breakdown in CIDP initiates autoimmune infiltration. Activated T cells and their secreted cytokines disrupt endothelial tight junctions in the BNB, allowing entry of inflammatory cells into the . This loss of barrier integrity, observed across CIDP subtypes via enhanced permeability and protein leakage, sets the stage for localized immune responses targeting myelin sheaths. T-cell infiltration follows BNB compromise, with CD4+ and CD8+ T cells accumulating at sites of in CIDP patients. These cells contribute to the inflammatory milieu by releasing proinflammatory cytokines, including elevated TNF-α levels detected in (CSF) and serum during active disease phases. TNF-α correlates with clinical severity, promoting further recruitment of immune effectors and amplifying tissue damage through sustained activation of local immune cascades. Macrophages, recruited subsequent to T-cell driven , execute primary demyelination via segmental stripping of sheaths, as evidenced in biopsies from CIDP cases. Electron microscopy reveals macrophages extending processes into intact lamellae, selectively stripping segments without initial Schwann cell injury, leading to conduction block. This macrophage-mediated mechanism predominates in typical CIDP pathology, distinguishing it from primary axonal damage and underscoring cellular immunity's role in perpetuating chronic demyelination.

Role of autoantibodies and complement

In subsets of chronic inflammatory demyelinating polyneuropathy (CIDP), autoantibodies of the IgG class target proteins at the and paranodal regions, such as neurofascin-155 (NF155), disrupting axo-glial interactions essential for stability and nerve conduction. These antibodies, detected in approximately 10% of CIDP cases, bind to the NF155-contactin-1 complex at paranodal loops of Schwann cells, impairing the adhesion between axons and sheaths. IgG4-predominant forms predominate in anti-NF155-positive CIDP, often correlating with atypical features like and poor response to intravenous immunoglobulin (IVIG), though IgG3 subclasses against pan-neurofascin isoforms have been linked to more aggressive disease courses and complement recruitment. Complement activation amplifies humoral pathology in CIDP, with deposition of components like fragments and the membrane attack complex () observed in biopsies from affected patients. A 2025 immunohistochemical analysis of 55 specimens from CIDP and variant cases revealed marked complement involvement, including C3d and immunoreactivity colocalizing with demyelinated fibers, suggesting innate immune escalation beyond adaptive effects. This deposition promotes recruitment and demyelination, independent of cellular infiltrates in some subsets, and aligns with therapeutic rationale for complement inhibitors in refractory disease. IgG3 autoantibodies, by virtue of their ability to fix complement via C1q binding, may preferentially drive this pathway in or treatment-resistant presentations, contrasting with non-complement-activating IgG4 forms. Empirical data from cohort studies indicate such subclass-specific activation correlates with IVIG non-response, underscoring humoral-complement interplay in disease persistence.

Cellular and molecular processes in demyelination

In CIDP, demyelination primarily involves macrophage-mediated stripping of sheaths from axons, executed through direct penetration of the -axon unit, resulting in focal disruption of compact . This process targets internodal regions, leading to segmental demyelination characterized by widened nodes of Ranvier and exposure of paranodal structures, which impairs and manifests as conduction blocks due to dysfunction. Schwann cells respond to demyelination by , , and attempted remyelination, forming nascent sheaths that are often thinner and shorter than normal, as observed in biopsies showing excessive folding and incomplete internodal lengths. However, chronic immune pressure reduces plasticity, hindering effective repair and contributing to persistent conduction abnormalities, with histopathological evidence of ongoing cycles of demyelination and partial remyelination in teased fiber preparations. Serial nerve biopsy data reveal recurrent demyelinating events interspersed with abortive remyelination, evidenced by increased onion bulb formations—concentric arrays of dedifferentiated Schwann cells—correlating with relapsing clinical courses and failure to achieve stable conduction restoration. These molecular alterations, including disrupted expression of myelin proteins like and PMP22 in regenerating Schwann cells, underscore the inefficiency of repair mechanisms under sustained inflammatory conditions. Prolonged demyelination in untreated CIDP triggers secondary axonal degeneration, initiated by Wallerian-like breakdown distal to demyelinated segments, with studies documenting axonal loss in up to 83.7% of cases and clinical observations indicating accumulation of irreversible damage within months of onset if is delayed. Empirical thresholds suggest that axonal integrity deteriorates significantly after 6-12 months of unchecked disease activity, shifting the pathology from potentially reversible demyelination to permanent neuropathy.

Diagnosis

Clinical and electrophysiological criteria

The diagnosis of chronic inflammatory demyelinating (CIDP) requires fulfillment of standardized criteria outlined in the 2021 European Academy of Neurology/Peripheral Nerve Society (EAN/PNS) guideline, which emphasize clinical features of motor involvement, electrophysiological demonstration of acquired demyelination in peripheral nerves, and exclusion of alternative disorders such as hereditary neuropathies, monoclonal gammopathies, or diabetic . These criteria simplify prior classifications by reducing diagnostic certainty levels to CIDP or possible CIDP, prioritizing objective evidence of multifocal demyelination over treatment response to minimize misdiagnosis risks. For typical CIDP, clinical inclusion mandates a progressive or relapsing course over at least 8 weeks, featuring symmetric proximal and distal in upper and lower limbs, with optional but areflexia or required in all extremities. Proximal weakness distinguishes typical cases from distal-predominant variants and is essential for confirming motor involvement. (CSF) analysis supports diagnosis when protein exceeds 45 mg/dL (0.45 g/L) without pleocytosis (<10 cells/μL), though normative values may rise to >60 mg/dL in patients over 50 or with comorbidities like . Electrophysiological confirmation demands abnormalities in at least two motor nerves indicative of demyelination, including:
  • Distal motor prolongation ≥50% above the upper limit of (ULN),
  • Motor conduction reduction ≥30% below the lower limit of (LLN),
  • Prolonged F-wave ≥20% above ULN (or ≥50% if [CMAP] amplitude <80% LLN),
  • Conduction block with ≥50% CMAP amplitude reduction across a stimulated segment (or ≥30% for tibial nerve) without excessive temporal dispersion, or
  • Absent F-waves in two nerves if CMAP ≥20% LLN, combined with one other demyelinating parameter.
Sensory nerve studies typically show prolonged latencies or reduced velocities in at least two nerves, though motor criteria predominate; sural sparing may occur in early or variant forms. Possible CIDP applies when motor demyelination criteria are met in only one nerve alongside supportive features like elevated CSF protein, addressing equivocal electrophysiology to mitigate underdiagnosis, as validation cohorts indicate the 2021 criteria maintain high specificity (84-96%) while enhancing inclusivity for borderline cases compared to 2010 standards. Exclusion of mimics remains mandatory, incorporating red flags such as prominent cranial nerve involvement, systemic malignancy, or hereditary patterns absent in CIDP.

Supportive tests and imaging

Cerebrospinal fluid (CSF) analysis serves as a key supportive test in CIDP, classically showing cytoalbuminologic dissociation with elevated protein levels (typically >45 mg/dL) and a low count (<10 cells/µL). This pattern, present in 80-95% of typical cases, reflects disruption of the blood-nerve barrier at the nerve roots without substantial CSF inflammation, distinguishing it from conditions with pleocytosis such as infectious meningitides or Guillain-Barré syndrome variants. Elevated protein arises from leakage of serum proteins across inflamed root meninges, while the paucity of cells underscores the peripheral nerve focus of the pathology. Nerve ultrasound reveals multifocal enlargement of peripheral nerves, quantified by increased cross-sectional area (CSA), often >9 mm² at sites like the in the upper arm or elbow. This proximal-predominant swelling, with hypoechoic fascicles and preserved , yields a of approximately 80% in meta-analyses for confirming demyelinating features in suspected CIDP. The ultrasound pattern—diffuse rather than focal entrapment-like—correlates with disease activity and helps validate nerve involvement beyond . Magnetic resonance imaging (MRI) of the lumbosacral spine or commonly demonstrates hypertrophy and T2-weighted , with enhancement indicating active in roughly 70% of patients. Enhancement of the or plexus roots signals blood-nerve barrier permeability due to immune attack, a dynamic feature absent in static hereditary neuropathies despite their potential for enlargement. These findings, best visualized post-contrast, provide visual corroboration of radiculoneuropathic involvement and track response through serial imaging.

Differential diagnosis and misdiagnosis risks

CIDP requires differentiation from Guillain-Barré syndrome (GBS), an acute inflammatory neuropathy characterized by rapid symptom progression peaking within 4 weeks, in contrast to CIDP's insidious onset and course exceeding 8 weeks. (MMN) mimics CIDP through demyelinating motor deficits but features focal, asymmetric weakness without prominent sensory loss or symmetric involvement. Hereditary conditions such as Charcot-Marie-Tooth disease present with lifelong progression, positive family history, and genetic mutations, lacking the relapsing-remitting pattern and inflammatory response seen in CIDP. Diabetic polyneuropathy often simulates CIDP's distal symmetric symptoms but typically evolves as a length-dependent axonal process tied to duration, without the proximal weakness or rapid treatment responsiveness of CIDP. Paraproteinemic demyelinating neuropathies, associated with monoclonal gammopathies, can overlap clinically but are distinguished by serum paraproteins and poorer prognosis, necessitating exclusion to avoid conflating immune-mediated and dysproteinemic etiologies. Misdiagnosis occurs in up to 50% of referred cases, particularly with atypical variants or over-reliance on supportive features without rigorous progression assessment, leading to unnecessary exposure and its risks. is prevalent in elderly patients with comorbidities, where CIDP is erroneously attributed to age-related or compressive neuropathies, with referral cohorts showing 47% failing minimal criteria on review. Underdiagnosis risks arise when chronic progression is dismissed as irreversible diabetic or hereditary neuropathy, delaying in responsive cases. Nerve aids resolution in ambiguous scenarios by confirming inflammatory demyelination absent in mimics, though its utility varies by clinical suspicion.

Treatment

First-line immunomodulatory approaches

Intravenous immunoglobulin (IVIG) is a strongly recommended first-line immunomodulatory for CIDP, administered typically as an induction dose of 2 g/kg body weight divided over 2-5 days, followed by maintenance infusions of 1 g/kg every 3 weeks. The Intravenous Immunoglobulin in Chronic Inflammatory Demyelinating Polyradiculoneuropathy (ICE) trial, the largest (RCT) in CIDP involving 117 patients, demonstrated significant short-term improvement in muscle strength and scores within 2-6 weeks compared to , with sustained benefits in responders during a 24-week maintenance phase where approximately 70% of patients maintained or improved. IVIG's rapid onset of action, often within days, is attributed to mechanisms including saturation of the neonatal (FcRn), which accelerates of pathogenic autoantibodies, alongside effects on macrophages and complement inhibition. Corticosteroids, such as pulsed high-dose dexamethasone (40 mg daily for 4 days every 4 weeks for 6 cycles) or daily prednisolone (60 mg tapering over months), serve as an alternative first-line option, particularly when IVIG is unavailable or contraindicated. In the PREDICT RCT comparing pulsed dexamethasone to standard prednisolone in 40 patients, both regimens yielded similar short-term response rates around 80%, though long-term remission occurred in only about 30% of responders, with corticosteroids associated with higher relapse rates upon tapering compared to IVIG. A retrospective analysis reported a 61% response rate to corticosteroids with a 33% probability of sustained remission, but side effects including , , and limit their preference over IVIG in many cases. Plasma exchange (PE), involving 200-250 mL/kg over 5 sessions in the first 2 weeks, is recommended for acute exacerbations or as an initial therapy equivalent to IVIG in severe cases. The Dyck et al. RCT of 1989, randomizing 17 CIDP patients, found no significant difference in strength improvements between PE and IVIG after 2 weeks, with both achieving responses in over 70% of participants, supporting PE's role via removal of circulating humoral factors like autoantibodies. PE is typically reserved for rapid deterioration due to its invasiveness and lack of home administration feasibility compared to IVIG.

Second-line therapies and maintenance

For patients with chronic inflammatory demyelinating polyneuropathy (CIDP) refractory to first-line therapies such as intravenous immunoglobulin (IVIg), corticosteroids, or plasma exchange, second-line options include rituximab, particularly in cases associated with specific autoantibodies. Rituximab, a targeting CD20-positive B cells, has demonstrated efficacy in observational and open-label studies for refractory CIDP, with prospective data indicating clinical improvement in patients unresponsive to initial treatments. In variants involving autoantibodies against contactin-1, second-line rituximab has led to sustained stabilization or improvement in approximately 50% of cases, based on cohort analyses. However, a in broader CIDP populations found rituximab no more effective than in preventing , underscoring its targeted utility in autoantibody-positive subsets rather than universal application. Immunosuppressive agents like and mycophenolate mofetil serve as steroid-sparing alternatives in refractory or maintenance settings, though evidence derives primarily from small series rather than large meta-analyses specific to CIDP. has achieved remission in nearly all treated patients (89%) in limited cohorts, supporting its role in sustaining response while minimizing dependence. Mycophenolate mofetil has similarly enabled improvement in case reports of steroid-refractory disease, often as an adjunct to reduce risk. These agents are positioned as adjunctive rather than standalone due to heterogeneous responses and the need for monitoring for myelosuppression or infections. Maintenance therapy emphasizes strategies to prevent while improving , with subcutaneous immunoglobulin (SCIG) emerging as a viable option over repeated IVIg infusions. The ADVANCE-CIDP 1 phase 3 trial demonstrated that facilitated SCIG (fSCIG) at 10% concentration more effectively prevented relapse than in IgG-dependent patients, with sustained efficacy over 24 weeks. Long-term extension data from ADVANCE-CIDP 3 confirmed low relapse rates (under 10%) and favorable tolerability with fSCIG as maintenance, reducing infusion frequency and healthcare burden compared to intravenous routes. This approach is particularly suited for stable patients, allowing home administration and equivalent serum IgG levels to IVIg in meta-analyses of autoimmune neuropathies. Individual dosing titration remains essential to match prior IVIg requirements and avert deterioration.

Emerging treatments and clinical trials

Subcutaneous efgartigimod, an FcRn inhibitor, reduces IgG levels by blocking IgG recycling and has shown in CIDP through accelerated clearance of pathogenic autoantibodies. In the phase 3 ADHERE (NCT04281472), patients with CIDP who improved on open-label efgartigimod were randomized to continued treatment or ; 61% on efgartigimod remained relapse-free at week 24 versus 41% on , with rapid improvements in muscle strength and scores observed as early as week 4.00309-0/fulltext) The U.S. FDA approved subcutaneous efgartigimod (Vyvgart Hytrulo) for CIDP on June 21, 2024, based on these results, marking the first approval in this class for the condition. A phase 4 is underway to assess transitioning stable patients from intravenous immunoglobulin to efgartigimod, though some reports note risks of early deterioration during switches. 00449-0/abstract) Complement inhibitors targeting the innate immune pathway are under investigation for CIDP subsets with prominent complement deposition on nerve biopsies. Riliprubart, a C1s inhibitor acting upstream in the classical pathway, is in two phase 3 trials (VITALIZE and MOBILIZE; NCT06290128) comparing it to IVIg as first-line or add-on therapy in adults with CIDP, with primary endpoints of sustained improvement in adjusted inflammatory neuropathy cause and treatment scores over 24-52 weeks. Phase 2 data from 2024 demonstrated superior grip strength gains and a 35% reduction in neurofilament light chain levels versus IVIg, suggesting decreased axonal damage, with enrollment ongoing into 2025. Zilucoplan, a C5-targeting cyclic peptide, is explored in open-label studies for its potential to inhibit terminal complement activation, though larger efficacy data remain preclinical or early-stage as of 2024. BTK inhibitors, which modulate B-cell signaling and innate immunity, lack dedicated phase 2/3 trials in CIDP as of 2025, with repurposing discussions limited to preclinical rationale from models showing reduced macrophage activation. Ongoing research emphasizes personalized approaches based on profiles to identify responders among cases.

Prognosis

Short-term and long-term outcomes

In studies of patients with chronic inflammatory demyelinating polyneuropathy (CIDP), short-term outcomes following first-line immunomodulatory therapies such as intravenous immunoglobulin (IVIg) or corticosteroids demonstrate initial clinical in 70-80% of cases, typically within 2-4 weeks of initiation, as measured by improvements in disability scores like the Inflammatory Neuropathy Cause and Treatment () scale. Response rates vary by agent, with IVIg achieving 54-92% efficacy and corticosteroids around 60%, though improvements are often partial and require ongoing therapy to sustain gains. Long-term outcomes reveal a relapsing-remitting pattern in many patients, with rates exceeding 80% upon discontinuation of effective therapies like 6-month IVIg courses, often occurring within months and leading to renewed . Axonal loss, evident on conduction studies at , correlates with irreversible deficits, contributing to persistent weakness and sensory impairment despite demyelination reversal. Pooled data from multicenter analyses indicate that approximately 8% of patients become nonambulatory over extended follow-up, reflecting cumulative axonal damage rather than ongoing inflammation alone. Mortality in CIDP remains low at 3-5% across cohorts, attributable primarily to secondary complications such as infections from immunosuppressive therapies or respiratory involvement, rather than direct neuropathic progression. Case fatality analyses confirm this rate, with deaths rarely linked to the underlying demyelination process itself.

Prognostic factors and complications

Initiation of first-line immunomodulatory therapy within one year of symptom onset is independently associated with lower post-treatment scores and greater improvement in conduction amplitudes in multivariate analyses of long-term cohorts. Delays beyond this window correlate with accelerated axonal degeneration and irreversible deficits, as pretreatment fiber loss at strongly predicts sustained impairment independent of demyelinating features. Older age at onset (>50 years) emerges as an adverse predictor in models, linked to diminished regenerative capacity and altered immune that hampers recovery from demyelination. Axonal predominant variants, identified via conduction studies showing reduced amplitudes over conduction block predominance, confer worse odds ratios for persistent in multivariate logistic models from multicenter studies. Seropositive subsets with autoantibodies targeting nodal proteins (e.g., neurofascin-155 or contactin-1) demonstrate courses, with real-world data from 2020-2024 indicating response rates to initial IVIG or steroids around 40%, versus 70-80% in seronegative typical CIDP, per longitudinal analyses of treatment failures. Treatment complications arise primarily from prolonged . Corticosteroids, used in up to 50% of maintenance regimens, elevate risk through loss, with incidence rates exceeding 20% in long-term users per randomized comparisons. Immunomodulators like IVIG or plasma exchange carry infusion-related infections at 5-10% per cycle, while second-line agents (e.g., rituximab) heighten susceptibility, including rare cases in profoundly immunosuppressed patients. These risks underscore the need for monitoring in multivariate prognostic stratification, where cumulative therapy exposure modulates secondary morbidity beyond primary disease progression.

Epidemiology

Incidence and prevalence data

Chronic inflammatory demyelinating polyneuropathy (CIDP) has an estimated annual incidence of 0.15 to 1.6 cases per 100,000 person-years in -based studies, with pooled crude rates around 0.33 per 100,000 person-years across multiple registries. These figures derive primarily from Western cohorts using standardized diagnostic criteria such as the of Neurological Societies/Peripheral Nerve Society guidelines, though individual studies report variability, such as 0.68 per 100,000 person-years in a Welsh registry. Higher rates, up to 3.58 per 100,000 patient-years in some U.S. healthcare claims data, may reflect ascertainment bias from improved diagnostics rather than true increases. Prevalence estimates range from 0.67 to 10.3 cases per 100,000 individuals, influenced by the stringency of diagnostic criteria and study methodology. Broader criteria, including atypical variants, yield higher figures like 7.00 per 100,000, while stricter electrodiagnostic requirements produce lower rates around 2.95 per 100,000. Longitudinal data from and U.S. surveillance systems spanning the 1990s to indicate relative stability in these metrics within developed regions, suggesting consistent occurrence absent major environmental shifts. Underreporting likely prevails in developing regions due to limited neurological expertise and diagnostic access, as evidenced by sparser data from non- registries compared to comprehensive networks. Empirical from U.S. and sources highlights age-related patterns, with incidence rising from low rates in youth (e.g., 0.06 per 100,000 under age 20) to peaks in and beyond, though global registries remain incomplete for bimodal confirmation.

Demographic patterns and risk distributions

Chronic inflammatory demyelinating polyneuropathy (CIDP) demonstrates a consistent predominance across multiple population-based studies, with male-to-female ratios typically ranging from 1.5:1 to 2:1, though some reports indicate ratios up to 4:1. This disparity may reflect genuine sex-based differences in susceptibility, potentially linked to occupational exposures more common in s or variations in , though direct causal mechanisms remain unestablished and warrant scrutiny beyond diagnostic reporting biases. The condition's onset peaks between ages 40 and 60, with incidence rates increasing progressively with age, particularly elevating after 50 years, consistent with cumulative environmental or immune triggers over time rather than solely age-related diagnostic vigilance. Mean age at diagnosis often exceeds 50 years, as evidenced by cohorts reporting averages of 58 years, underscoring a toward later-life presentation that aligns with empirical patterns in autoimmune neuropathies but invites causal analysis of lifelong exposures over mere detection artifacts. Prevalence appears higher among Caucasians compared to Asians, with estimates of 10.15 per 100,000 in populations versus 2.64 per 100,000 in those of Asian descent, and similarly reduced rates in South Asian subgroups relative to non-Asians in data. These ethnic variations raise questions of genetic versus environmental causality, as comparative studies from report lower overall figures around 3.3 per 100,000, potentially confounded by diagnostic criteria stringency or healthcare access disparities rather than inherent population differences. Geographic distributions show minimal urban-rural gradients in reported cases, with no robust evidence of true disparities after accounting for improved urban diagnostics that may inflate apparent rates without indicating rising incidence. Predominantly studied in Western cohorts, global patterns suggest stable absent strong latitudinal or regional environmental drivers, though underdiagnosis in resource-limited areas could mask variations.