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Ciprofol

Ciprofol, chemically known as (R)-2-[(1-cyclopropyl)ethyl]-6-(propan-2-yl)phenol or HSK3486, is a short-acting intravenous anesthetic agent and sedative-hypnotic that functions as a positive allosteric modulator of the γ-aminobutyric acid type A (GABA_A) receptor, facilitating chloride ion influx to inhibit neuronal activity and induce rapid sedation or anesthesia. As a 2,6-disubstituted phenol derivative structurally modified from propofol, it exhibits 4- to 5-fold higher binding affinity to GABA_A receptors, enabling lower effective doses while providing a quick onset (T_max of 2-3 minutes) and metabolism primarily via CYP2B6 and UGT enzymes, with a half-life of approximately 2.09 hours and predominant renal excretion. Developed by China's Haisco Pharmaceutical Group and first reported in 2017, ciprofol received initial approval from the (NMPA) on December 15, 2020, for during gastrointestinal endoscopic procedures such as painless and gastroscopy. Subsequent expansions in 2022 broadened its indications to include and of general in surgical settings and for mechanically ventilated patients in intensive care units, positioning it as a versatile option for procedural and care primarily in , with approvals limited to as of November 2025 while investigational internationally. Ongoing clinical trials continue to evaluate its efficacy in diverse populations, including and obese patients, with phase III studies demonstrating its potential for broader applications. In clinical practice, ciprofol offers advantages over , including significantly reduced injection pain (incidence of 4.9% versus 52.4%), lower rates of respiratory depression (2.8% versus 5.5%), and enhanced hemodynamic stability with minimal cardiovascular effects, while achieving comparable depths and higher patient satisfaction scores in procedures like gastroscopy. Its higher potency allows for dose reductions of up to 50-70%, potentially mitigating common propofol-related adverse events such as and apnea, though it may involve slightly longer recovery times in some contexts. These properties have spurred interest in ciprofol as a safer alternative for short-duration and , particularly in high-risk patients, with research emphasizing its favorable safety profile in non-operating room settings.

Chemical properties

Structure

Ciprofol, chemically known as 2-[(1R)-1-cyclopropylethyl]-6-(propan-2-yl)phenol, has the molecular formula C14H20O and a of 204.31 g/mol. It is an optically active 2,6-disubstituted derivative, characterized by a cyclopropylethyl at the 2-position that introduces and enhances steric hindrance compared to its precursor. This structural feature contributes to greater in its interactions with biological targets. Ciprofol shares a phenolic core with , a 2,6-diisopropylphenol, but features a targeted replacement of one isopropyl group with the cyclopropylethyl moiety, which modifies its and overall pharmacological profile for potentially improved potency and fewer side effects. This design leads to a higher to relevant receptors.

Physical characteristics

Ciprofol, in its pure form, is a substance. Due to its high , indicated by a calculated value of approximately 4.37, ciprofol exhibits poor in but is soluble in organic solvents such as DMSO (up to 100 mg/mL). This , greater than that of ( 3.93), necessitates its formulation as an oil-in-water for intravenous administration, incorporating medium- and long-chain triglycerides. The commercial emulsion formulation of ciprofol appears as a white, opalescent, uniform liquid with no visible precipitation or under conditions. It maintains physical , with mean below 200 nm and relative deviation less than 1.0%, when stored at room temperature (25°C) or refrigerated (4°C) for up to 24 hours, and even at 37°C. The emulsion's is approximately 7.76, fluctuating minimally (≤0.07 units) over time, while remains around 321 mOsm/kg. Protection from light is recommended during to preserve , consistent with guidelines for similar emulsions.

Clinical uses

Approved indications

Ciprofol (also known as HSK3486) received approval from the National Medical Products Administration (NMPA) on December 15, 2020, for use as a short-acting intravenous agent specifically for during endoscopic procedures, including gastrointestinal (such as gastroscopy and ) and , in adults. This initial indication targets moderate to facilitate painless examination and intervention, allowing for rapid onset and recovery suitable for outpatient settings. In 2021, the NMPA expanded the approved indications to include and of general in surgical settings (approval number H20210007), with typical dosing of 0.4 mg/kg bolus for followed by as needed. In July 2022, the NMPA further expanded approval to include for (ICU) patients requiring , addressing the need for prolonged in critically ill individuals while minimizing hemodynamic instability. For procedural in , such as gastroscopy, , and , ciprofol is typically administered as a single intravenous bolus dose of 0.4–0.5 mg/kg, achieving effective within 1–2 minutes. In ICU settings, dosing involves an initial loading of 0.1–0.2 mg/kg over 0.5–5 minutes, followed by a starting at 0.3 mg/kg/h, titrated to maintain a target level (e.g., of –2 to 0). Clinical studies supporting these approvals demonstrate that ciprofol provides comparable sedation efficacy to but with advantages in recovery profiles, including shorter times to full alertness and orientation after gastrointestinal procedures, attributed to its higher potency and favorable as a GABA_A receptor agonist.

Investigational applications

A multicenter phase III trial in demonstrated ciprofol's non-inferiority to for and in outpatient gynecological procedures, such as , achieving high success rates with reduced injection pain and adverse events. Additionally, clinical studies have explored its use in , where ciprofol provided effective induction and maintenance of with stable and a 100% success rate, comparable to . Research into ciprofol's neuroprotective potential focuses on its combination with mild therapeutic following . Preclinical studies in rat models showed that ciprofol, when paired with , improved survival rates and neurological outcomes by reducing brain injury markers, supporting its hypothesis as an adjunct for post-arrest in humans. Investigational applications in special populations include pediatric and elderly patients. In children aged 3–12 years, trials established the effective dose (ED50) of ciprofol for induction at approximately 0.35 mg/kg without , demonstrating rapid onset, stable circulation, and low incidence of injection pain during procedures like adenotonsillectomy. For elderly patients undergoing thoracic surgery, randomized controlled trials indicated that ciprofol reduced the incidence of postoperative compared to , with lower rates of cognitive fluctuations and improved recovery profiles in major procedures. Comparative studies from 2024–2025 highlight ciprofol's advantages over in obese patients, particularly for hemodynamic stability during induction. In randomized trials involving obese individuals undergoing gastrointestinal or laparoscopic surgery, ciprofol-remifentanil combinations maintained superior and stability, with fewer respiratory adverse events and better overall safety profiles than propofol equivalents.

Adverse effects

Common reactions

Common adverse reactions to ciprofol are generally mild to moderate and include , , and mild respiratory , which occur dose-dependently and resolve quickly due to the drug's short of approximately 2-3 hours. In clinical trials for , has been reported in 19-26% of patients receiving ciprofol, typically manifesting as a transient decrease in without requiring intervention in most cases. , defined as below 60 beats per minute, occurs in 8-39% of patients, with higher rates at doses compared to maintenance . Mild respiratory , such as transient desaturation, is observed in less than 10% of cases, often self-limiting and less frequent than with . Injection site reactions are minimal with ciprofol, with pain on injection reported in under 5% of patients—significantly lower than the 30-50% incidence seen with due to ciprofol's modified . Other common effects include transient and , affecting 1-5% of patients postoperatively, which typically resolve within minutes to hours owing to the drug's rapid . Management of these reactions is primarily supportive and dose-related; lower infusion rates for (e.g., 0.4-0.8 mg/kg/h) result in reduced incidence compared to bolus doses (e.g., 1.5-2 mg/kg), allowing for safer use in outpatient procedures. Overall, the profile of common reactions supports ciprofol's tolerability in clinical settings, with rates often comparable or lower than in randomized trials.

Serious risks

Ciprofol administration carries risks of or apnea, particularly during high-dose induction for general , though the incidence remains low at approximately 3% in procedural sedation contexts, significantly less than the 10% observed with . These events necessitate close monitoring of respiratory function and readiness for ventilatory support, as they can lead to if unmanaged. Cardiovascular collapse, manifesting as severe or arrhythmias, poses a serious , especially in patients with pre-existing cardiac conditions such as or severe valvular disease. Ciprofol is contraindicated in cases of known to the drug or its components, and extreme caution is advised in severe cardiac impairment to avoid exacerbating hemodynamic instability. Studies indicate a lower overall incidence of with ciprofol compared to , but vulnerable patients may still require dose titration and cardiovascular monitoring. Allergic reactions, including rare , can occur due to the lipid emulsion formulation containing and , similar to propofol-related . Such reactions demand immediate intervention with epinephrine and supportive care, underscoring the need for pre-administration screening. In special populations, caution is warranted. Elderly patients exhibit heightened sensitivity, necessitating a reduced induction dose of 0.3 mg/kg to minimize risks of respiratory and hemodynamic adverse effects. For pregnant individuals, data are limited, and use is recommended only if benefits outweigh potential risks, with no established safety profile. In cases of mild renal or hepatic impairment, no dose adjustment is required, as ciprofol's pharmacokinetics remain unaffected; however, monitoring is advised for moderate to severe cases.

Pharmacology

Pharmacodynamics

Ciprofol, the R-enantiomer, acts primarily as a positive of γ-aminobutyric acid type A () receptors, enhancing the binding of the endogenous to these ligand-gated ion channels. This potentiation increases ion influx into neurons, resulting in membrane hyperpolarization and subsequent inhibition of neuronal excitability, which underlies its and effects. Compared to , ciprofol demonstrates 4- to 5-fold greater potency, attributed to its higher binding affinity for GABAA receptors containing the β3 subunit, as evidenced by simulations showing stronger interactions of the R-enantiomer of ciprofol with GABRB3. This enhanced affinity contributes to its efficacy at lower doses while maintaining a favorable safety profile. Ciprofol exhibits high selectivity for GABAA receptors, with minimal interaction at non-GABAA targets such as sodium, potassium, or calcium channels, which reduces the incidence of cardiovascular and respiratory depression relative to . In dose-response studies, the median effective dose (ED50) for is approximately 0.4 mg/kg. Preclinical models have revealed mild anti-inflammatory properties of ciprofol, including attenuation of activation in mouse models and reduction of pro-inflammatory cytokines in ischemia-reperfusion injury.

Pharmacokinetics

Ciprofol is administered exclusively via intravenous injection or infusion, achieving complete due to this route. Its high facilitates rapid , typically within 30 to 60 seconds following administration, allowing quick penetration into the . Following administration, ciprofol exhibits extensive throughout the body, characterized by a large of approximately 3 to 4 L/kg, reflecting its partitioning into tissues such as the and . It rapidly redistributes from the to peripheral compartments, contributing to its short duration of effect. is high, around 95% to 99%, primarily to , which influences its free fraction availability. Ciprofol undergoes primary hepatic metabolism through phase II conjugation, predominantly via the enzyme UDP-glucuronosyltransferase 1A9 (UGT1A9), forming inactive metabolites such as M4. The pathway via UGT1A9 accounts for the majority (~54%) of , with contributing ~24.5%. The metabolites lack activity, ensuring that pharmacological effects are attributable to the parent compound. Elimination of ciprofol is characterized by a of 2 to 3 hours, supporting its suitability for short procedures without prolonged recovery. The drug and its metabolites are primarily excreted via the kidneys, with over 80% of the dose recovered in urine as the conjugate M4 within 24 hours and negligible amounts of unchanged parent drug. No significant accumulation occurs with repeated or continuous dosing, owing to its efficient clearance.

Development and regulation

History

Ciprofol (HSK3486) was developed by Haisco Pharmaceutical Group Co., Ltd., based in , , and first reported in 2017, as a of intended to address key limitations such as injection site pain and hemodynamic instability. This innovation stemmed from efforts to create a short-acting intravenous with enhanced selectivity for the GABA_A receptor while minimizing cardiovascular and respiratory depression. Preclinical studies evaluated ciprofol in animal models including rats and dogs, confirming its and effects through metrics like loss of righting reflex (LORR). These investigations revealed that ciprofol exhibited approximately 4- to 6-fold greater potency compared to (ED50 for LORR in rats: 0.88 mg/kg versus 5.05 mg/kg for propofol) alongside a more favorable safety profile, including reduced cardio-depressive effects and no injection pain. Initial pharmacokinetic data from these studies supported rapid onset and offset, paving the way for clinical advancement. Early human trials commenced with Phase I studies in in 2018, which assessed safety, tolerability, and in healthy volunteers across doses up to 0.81 mg/kg without reaching dose-limiting . Phase III trials in , conducted from 2018 to 2019, focused on efficacy for procedures like and demonstrated non-inferiority to with fewer adverse reactions. Regulatory milestones accelerated thereafter: Haisco submitted a to China's (NMPA) in 2020, leading to initial approval on December 15, 2020, for during gastrointestinal (approval H20200013). Approval for induction and maintenance of general followed in 2021 (approval H20210007). An extension for in patients requiring was granted in July 2022. As of 2025, a phase III trial in (NCT05486416, completed in 2024) supports further regulatory pursuits, with ongoing evaluations in surgical and procedural settings.

Approval status

Ciprofol, also known as HSK3486, received approval from the (NMPA) in for sedation during gastrointestinal on December 15, 2020. In July 2022, the NMPA expanded its approval to include sedation for patients requiring in intensive care units. It is marketed in exclusively as Sishuning (Ciprofol Injection), a 2 mg/mL formulation developed and commercialized by Haisco Pharmaceutical Group Co., Ltd. No generic versions of ciprofol are currently available worldwide. Outside of , ciprofol remains investigational and has not received regulatory approval as of November 2025. , phase III clinical trials are ongoing for indications such as and general in outpatient procedures, with no FDA approval granted to date. Phase I trials were conducted in in 2018, while phase III trials continue in the United States (e.g., NCT05486416, completed in 2024). Ciprofol is not approved in any other countries, including or , despite market interest in the region. Access to ciprofol is limited to approved clinical use within hospitals for the specified indications, where it is administered intravenously under supervision. Globally, availability is restricted to investigational settings through ongoing clinical trials, and it holds no over-the-counter status anywhere. In trial contexts, it is commonly referred to by its developmental code HSK3486 or the generic name ciprofol.